Whenever a child is sick, parents instinctively search out medicine or a cure. The task has been an unusually daunting one for John and Aileen Crowley. Two of their three children were diagnosed with a rare muscle-wasting disorder called Pompe disease. The affliction is so rare, that not only was there no medicine to treat it, but the big pharmaceutical companies weren’t even thinking about developing drugs for it.
So John Crowley did the only thing he could. He rounded up some scientists, hit up venture capitalists, and started a company to develop a drug to save his children’s lives. It’s been a draining five year odyssey, but earlier this year the Crowley children started their treatment.
Guests:
John and Aileen Crowley, parents of two children with Pompe disease. John launched a company to develop a cure.